B cell-intrinsic deficiency of the Wiskott-Aldrich syndrome protein (WASp) causes severe abnormalities of the peripheral B-cell compartment in mice.

نویسندگان

  • Mike Recher
  • Siobhan O Burns
  • Miguel A de la Fuente
  • Stefano Volpi
  • Carin Dahlberg
  • Jolan E Walter
  • Kristin Moffitt
  • Divij Mathew
  • Nadine Honke
  • Philipp A Lang
  • Laura Patrizi
  • Hervé Falet
  • Marton Keszei
  • Masayuki Mizui
  • Eva Csizmadia
  • Fabio Candotti
  • Kari Nadeau
  • Gerben Bouma
  • Ottavia M Delmonte
  • Francesco Frugoni
  • Angela B Ferraz Fomin
  • David Buchbinder
  • Emma Maria Lundequist
  • Michel J Massaad
  • George C Tsokos
  • John Hartwig
  • John Manis
  • Cox Terhorst
  • Raif S Geha
  • Scott Snapper
  • Karl S Lang
  • Richard Malley
  • Lisa Westerberg
  • Adrian J Thrasher
  • Luigi D Notarangelo
چکیده

Wiskott Aldrich syndrome (WAS) is caused by mutations in the WAS gene that encodes for a protein (WASp) involved in cytoskeleton organization in hematopoietic cells. Several distinctive abnormalities of T, B, and natural killer lymphocytes; dendritic cells; and phagocytes have been found in WASp-deficient patients and mice; however, the in vivo consequence of WASp deficiency within individual blood cell lineages has not been definitively evaluated. By conditional gene deletion we have generated mice with selective deficiency of WASp in the B-cell lineage (B/WcKO mice). We show that this is sufficient to cause a severe reduction of marginal zone B cells and inability to respond to type II T-independent Ags, thereby recapitulating phenotypic features of complete WASp deficiency. In addition, B/WcKO mice showed prominent signs of B-cell dysregulation, as indicated by an increase in serum IgM levels, expansion of germinal center B cells and plasma cells, and elevated autoantibody production. These findings are accompanied by hyperproliferation of WASp-deficient follicular and germinal center B cells in heterozygous B/WcKO mice in vivo and excessive differentiation of WASp-deficient B cells into class-switched plasmablasts in vitro, suggesting that WASp-dependent B cell-intrinsic mechanisms critically contribute to WAS-associated autoimmunity.

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WASP confers selective advantage for specific hematopoietic cell populations and serves a unique role in marginal zone B-cell homeostasis and function.

Development of hematopoietic cells depends on a dynamic actin cytoskeleton. Here we demonstrate that expression of the cytoskeletal regulator WASP, mutated in the Wiskott-Aldrich syndrome, provides selective advantage for the development of naturally occurring regulatory T cells, natural killer T cells, CD4(+) and CD8(+) T lymphocytes, marginal zone (MZ) B cells, MZ macrophages, and platelets. ...

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Wiskott-Aldrich syndrome protein deficiency in B cells results in impaired peripheral homeostasis

To more precisely identify the B-cell phenotype in Wiskott-Aldrich syndrome (WAS), we used 3 distinct murine in vivo models to define the cell intrinsic requirements for WAS protein (WASp) in central versus peripheral B-cell development. Whereas WASp is dispensable for early bone marrow B-cell development, WASp deficiency results in a marked reduction in each of the major mature peripheral B-ce...

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IMMUNOBIOLOGY B cell–intrinsic deficiency of the Wiskott-Aldrich syndrome protein (WASp) causes severe abnormalities of the peripheral B-cell compartment in mice

Mike Recher,1 Siobhan O. Burns,2,3 Miguel A. de la Fuente,1,4 Stefano Volpi,1 Carin Dahlberg,5 Jolan E. Walter,1 Kristin Moffitt,6 Divij Mathew,1 Nadine Honke,7 Philipp A. Lang,7 Laura Patrizi,1 Hervé Falet,8 Marton Keszei,9 Masayuki Mizui,10 Eva Csizmadia,11 Fabio Candotti,12 Kari Nadeau,13 Gerben Bouma,2 Ottavia M. Delmonte,1 Francesco Frugoni,1 Angela B. Ferraz Fomin,1 David Buchbinder,14 Em...

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WASp-deficient B cells play a critical, cell-intrinsic role in triggering autoimmunity

Patients with the immunodeficiency Wiskott-Aldrich syndrome (WAS) frequently develop systemic autoimmunity. Here, we demonstrate that mutation of the WAS gene results in B cells that are hyperresponsive to B cell receptor and Toll-like receptor (TLR) signals in vitro, thereby promoting a B cell-intrinsic break in tolerance. Whereas this defect leads to autoantibody production in WAS protein-def...

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WASP levels in platelets and lymphocytes of wiskott-aldrich syndrome patients correlate with cell dysfunction.

Wiskott-Aldrich syndrome, an inherited blood cell disorder due to mutations of the X-chromosome gene WASP (Wiskott-Aldrich syndrome protein), was characterized originally by thrombocytopenia, immunodeficiency, and eczema. Whereas platelet dysfunction is severe and consistent, immune defects are clinically variable, ranging from negligible to life threatening. To understand this heterogeneity, w...

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عنوان ژورنال:
  • Blood

دوره 119 12  شماره 

صفحات  -

تاریخ انتشار 2012